Concept of the "Orphan"drug

It must include:

1.) Summary of the article that is based off of the book “The cure” by Geeta Anand

2.) Give genetic and clinical aspects of the Pompe Disease

3.) Concept of the “Orphan”drug

4.) Roles of the Pharmaceutical companies and FDA in Drug Development

*THE ASSIGNMENT IS ACTUALLY SUPPOSE TO BE ON THE BOOK BUT I FOUND AN ARTICLE THAT HAS THE INFORMATION THAT IS NEEDED…SO IN THE REFERENCE PAGE DON’T USE THE ARTICLE AS A REFERENCE https://www.wsj.com/articles/SB106184568337857300